6th Annual KTRN Meeting

Attendees of 6th annual KTRN meeting

The annual Krabbe Translational Research Meeting, one of The Legacy of Angels Foundation’s signature grants was held at the beautiful conference facilities at the ‘Tween Waters Inn on Captiva Island February 3-5, 2016.

Again an international group of highly dedicated scientists gathered to advance research for krabbe’s always striving to accelerate the pace of better treatments from the bench to the bedside to improve outcomes for those affected by krabbe.

Led by Dr. Maria Escolar, the world-wide recognized leader in translational research for krabbe, robust discussions were ongoing for 2½ days. Ranging from new brain imaging (from another TLOAF funded grant) highlighting biomarkers that may be useful in newborn screening to new knowledge in pathology thanks to the recently developed Krabbe Brain Bank at the University of Pittsburgh (part of the TLOAF funded NDRD Infrastructure grant.)

The most exciting highlight was the dramatic results Dr. David Wenger presented on the increased lifespan and function of the Twitcher mice he is treating with bone marrow transplant and gene therapy (another TLOAF grant.)

Exciting research moving forward on all fronts was shared and we are thrilled, once again for the efforts of the work of the TLOAF grant funding.